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Good evening. This snapshot of stories and roundup is recommended just for you, based on your interests and reading history. | | | | (Children's Hospital of Philadelphia) | | | | | | | What to know Gene-editing technologies are transforming treatments for rare genetic disorders, but many therapies face hurdles in becoming accessible medicines. A study in the New England Journal of Medicine highlights successful gene therapy for ADA-SCID, yet commercialization challenges persist. Efforts to streamline regulations and develop new business models are underway to address these issues. Summary is AI-generated, newsroom-reviewed. What are your thoughts on the challenges faced by scientists in turning successful gene therapies from academic trials into approved medicines? | | | | Opinion Letters to the Editor | | | | How was today's newsletter? | | | | | | | | |